Bluebird Halts Gene-based Therapy Trials as Patients Diagnosed with Cancer—Stock Plummets
Two patients with sickle cell disease involved with a gene-based therapy trial now have been diagnosed with cancer, and the […]
UK’s NICE Rejects bluebird bio: Questions Value Price Tag & Nominal Clinical Evidence While Sponsor Shocked
A gene therapy for patients with transfusion-dependent beta thalassemia (TDT) didn’t fare well after a thorough review by the United […]
Gene-Therapy City: Philadelphia Biotech Ventured Continue Funding Wave with ‘Centyrins’ Developer Aro Biotherapeutics Secures $88m
A Philadelphia gene-therapy biotech venture just raised $88 million in investment from Johnson & Johnson and other investors, domestic and […]
Jeito Capital leads €20 Million Investment in InnoSkel, a New Gene Therapy Company and Leader in Rare Skeletal Disorders
Jeito Capital (“Jeito”), a rapidly emerging independent investor dedicated to biotech and biopharma, today announces that it has led a […]
CRISPR-based Gene Therapy Shows Initial Promise Targeting Sickle Cell Disease & Thalassemia
A painful inherited blood disorder affecting millions of people, especially Black people, occurs because of a deficiency of red blood […]
Axovant Gene Therapies Announces FDA Clearance of IND for AXO-AAV-GM2 Gene Therapy in Tay-Sachs and Sandhoff Diseases
Axovant Gene Therapies Ltd. (NASDAQ: AXGT), a clinical-stage company developing innovative gene therapies, today announced that the U.S. Food and […]
Bayer Acquires Gene Therapy Leader AskBio for up to $4 Billion Deal: Becoming a Global Gene Therapy Powerhouse
Germany-based Bayer acquired AskBio’s industry leading AAV-based gene therapy platform to accelerate its ability to bring urgently needed treatments to […]
Gene Therapy for Treatment of Limb-Girdle Muscular Dystrophy Type 2E Shows Sustained Promise 18 Months Post Admin
Sarepta Therapeutics, Inc. (NASDAQ: SRPT), positioning itself as a leader in precision genetic medicine for rare diseases, recently announced positive […]
Errant Gene Therapeutics (“EGT”) asks European Authorities to Re-examine the Approval Process of Zynteglo, While US Litigation Moves Forward
Picking up on the ongoing “Family Man” saga, in New York Court, EGT claims that Zynteglo, the Bluebird Bio product […]
Gene Therapy Startup Kriya Therapeutics Raised $80.5m in A Round & Now Announces Gene Therapy MFG Facility in RTP
Kriya Therapeutics announced today that it has secured a 51,350 square foot operational manufacturing facility in Research Triangle Park (RTP), North […]
