Sarepta Therapeutics along with partner Roche presented new analyses and functional data from several studies evaluating SRP-9001 (rAAVrh74.MHCK7.micro-dystrophin), a gene transfer therapy for patients with…
Boston-based Intergalatic Therapeutics has launched with $75 million in Series A financing from Advanced Technology Products Corporation (ATP). The funds will be used to advance Intergalactic’s breakthrough non-viral gene therapy platform, which utilizes two proprietary…
PTC Therapeutics presented an analysis of five-year data showing its novel gene therapy, PTC-AADC, leads to profound improvements in children with aromatic L-Amino acid decarboxylase (AADC)…
Pfizer recently sent a letter to a patient advocacy group called Parent Project Muscular Dystrophy (PPMD) indicating three serious adverse events reported in an ongoing study…
Scaling up the production of engineered cell therapies continues to represent a challenge for pervasive cell therapy advancement, but new ventures are sprouting to address the challenge…
Please confirm you want to block this member.
You will no longer be able to:
Please note: This action will also remove this member from your connections and send a report to the site admin. Please allow a few minutes for this process to complete.
