2019 was a promising year for cystic fibrosis (CF) patients as a new drug called Trikafta was approved by the FDA and can benefit up to 90% of the patient population. It works with those patients that share the most common mutation (delta-F508) to the CFTR gene. Local...
Trikafta
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Life or Death for Young Lady with Cystic Fibrosis—Trikafta Not Approved in UK & Europe and Time’s Running Out
28 year-old Nicole Adams from Belfast is literally being suffocated by her own body due to her case of cystic fibrosis. A wonder drug called Trikafta could potentially save her. The problem: although approved in America, it hasn’t been approved in Europe or the UK;...
FDA Approves New Breakthrough Therapy for Cystic Fibrosis
The U.S. Food and Drug Administration recently approved Vertex Pharmaceutical’s Trikafta (elexacaftor/ivacaftor/tezacaftor), the first triple combination therapy available to treat patients with the most common cystic fibrosis mutation. Trikafta is approved for...