Cystic Fibrosis


Margaret Rosenfeld, MD, MPH, Seattle Children’s Research Institute and Department of Pediatrics, University of Washington School of Medicine

Dr. Rosenfeld was a lead investigator in the Phase 3 ARRIVAL study, sponsored by Vertex, which found Ivacaftor (KALYDECO®) is generally safe and effective in patients aged 2 years and older who have cystic fibrosis and specific CFTR mutations. Dr. Rosenfeld noted...

Cystic Fibrosis Breakthrough Treatment Study

Kristi Rosa of RareDisease Report notes that over 70,000 are effected by cystic fibrosis and "although advances have been made in the fight against the progressive genetic disease which has allowed these patients to live longer lives, additional treatment options are...

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